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Insights into spinal muscular atrophy from molecular biomarkers

Xiaodong Xing Xinzhu Liu Xiandeng Li Mi Li Xian Wu Xiaohui Huang Ajing Xu Yan Liu Jian Zhang

Neural Regeneration Research2025,Vol.20Issue(7):P.1849-1863,15.
Neural Regeneration Research2025,Vol.20Issue(7):P.1849-1863,15.DOI:10.4103/NRR.NRR-D-24-00067

Insights into spinal muscular atrophy from molecular biomarkers

Xiaodong Xing 1Xinzhu Liu 2Xiandeng Li 1Mi Li 2Xian Wu 1Xiaohui Huang 2Ajing Xu 2Yan Liu 2Jian Zhang2

作者信息

  • 1. Department of Clinical Pharmacy,Xinhua Hospital,Shanghai Jiao Tong University School of Medicine,Shanghai,China College of Pharmacy,Chongqing Medical University,Chongqing,China
  • 2. Department of Clinical Pharmacy,Xinhua Hospital,Shanghai Jiao Tong University School of Medicine,Shanghai,China
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摘要

关键词

biomarkers/disease progression/gene-targeting therapy/neurofilaments/Nusinersen/spinal muscular atrophy(SMA)/survival motor neuron/therapeutic evaluation/treatment outcomes

分类

医药卫生

引用本文复制引用

Xiaodong Xing,Xinzhu Liu,Xiandeng Li,Mi Li,Xian Wu,Xiaohui Huang,Ajing Xu,Yan Liu,Jian Zhang..Insights into spinal muscular atrophy from molecular biomarkers[J].Neural Regeneration Research,2025,20(7):P.1849-1863,15.

基金项目

supported by the Collaborative Innovation Center for Clinical and Translational Science by Chinese Ministry of Education&Shanghai,No.CCTS-2022205 ()

the“Double World-Class Project”of Shanghai Jiaotong University School of Medicine(both to JZ)。 (both to JZ)

Neural Regeneration Research

1673-5374

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